It has been a remarkable year of promise in medical science.
Incurable diseases from sickle cell to haemophilia now look as though they can be treated. Here are the highlights.
Huntington’s
The defect that causes the devastating degenerative disease Huntington’s has been corrected in patients for the first time.
It has been called the biggest breakthrough in neurodegenerative diseases for 50 years.
The disease is caused by an aberration in a section of DNA called the huntingtin gene.
The error corrupts a healthy protein and turns it into a killer of brain cells.
The therapy silences the gene by blocking the messages it sends to the cell’s protein-making factories.
The study has generated a huge amount of excitement. It could be the first treatment to slow or prevent any degenerative brain disease.
Huntington’s breakthrough may stop disease
New skin
Hassan has been given a new genetically modified skin that covers 80% of his body.
He was born …
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